http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3956447-A1

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classificationIPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113
filingDate 2020-04-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_3d9df6c3c917246dbdf2c21e9106e768
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publicationDate 2022-02-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3956447-A1
titleOfInvention Antisense oligonucleotides for the treatment of usher syndrome
abstract The invention relates to the fields of medicine. In particular, it relates to novel antisense oligonucleotides (AONs) that are capable of skipping exon 62 from human USH2A premRNA and that may be used in the treatment, prevention and/or delay of Usher syndrome type II and/or USH2A -associated non syndromic retina degeneration.
priorityDate 2019-04-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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