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publicationDate 2022-01-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3937985-A1
titleOfInvention Gene therapy compositions and methods for treating parkinson's disease
abstract A method of improving motor function and reducing dyskinesia in a subject suffering from a neurodegenerative disease or a disease where endogenous dopamine levels are reduced in the subject comprising administering an effective amount of a viral vector comprising a nucleic acid construct comprising (i) a nucleotide sequence which encodes tyrosine hydroxylase (TH), (ii) a nucleotide sequence which encodes GTP-cyclohydrolase I (CH1), (iii) a nucleotide sequence which encodes Aromatic Amino Acid Dopa Decarboxylase (AADC), or any combination thereof to the subject.
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