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filingDate 2020-02-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_3cb003e11f5295124989ee492a073f1b
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_6092fe37692a88c6671949ffcc2b3d4d
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publicationDate 2021-12-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3923994-A1
titleOfInvention Compositions and methods for treating alpha-1 antitrypsin deficiency
abstract The present invention features compositions and methods for editing deleterious mutations associated with alpha-1 anti-trypsin (A1AT) deficiency. In particular embodiments, the invention provides methods for correcting mutations in an A1AT polynucleotide using an adenosine deaminase base editor, ABE8, having unprecedented levels of efficiency.
priorityDate 2019-02-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393714
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399167
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226520974
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226406004
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226426117
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID14251829
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226409512
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226425931
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226489581
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID66025
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID2901
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226489582
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135415876
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID54740249
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226565385
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395152

Total number of triples: 320.