http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3921430-A1

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filingDate 2020-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_a01f330e2db90362383a3c5d9e98f4f8
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publicationDate 2021-12-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3921430-A1
titleOfInvention Adeno-associated virus delivery of cln3 polynucleotide
abstract The present disclosure relates to recombinant adeno-associated virus (rAAV) delivery of a ceroid lipofuscinosis neuronal 3 (CLN3) polynucleotide. The disclosure provides rAAV and methods of using the rAAV for CLN3 gene therapy of the neuronal ceroid lipofuscinosis or CLN3 -Batten Disease.
priorityDate 2019-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59309
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO34425
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9541
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO52631
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226412983
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID11886
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ48335

Total number of triples: 320.