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filingDate 2013-06-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_3183fd923af2857b23ca3012469c4524
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publicationDate 2021-05-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3818991-A2
titleOfInvention Compositions and methods for treating diseases
abstract The present invention provides compositions and methods of use pertaining to rAAV- mediated delivery of therapeutically effective molecules for treatment of diseases such as Pompe disease. These compositions in combination with various routes and methods of administration result in targeted expression of therapeutic molecules in specific organs, tissues and cells.
priorityDate 2012-06-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID24186254
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID16759173
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7427

Total number of triples: 308.