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filingDate 2019-05-27-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_efeee686ef11116502d83a7a036dffd2
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publicationDate 2021-04-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3802803-A1
titleOfInvention Adenoassociated virus vectors for the treatment of mucopolysaccharidoses type iv a
abstract The present invention provides new polynucleotide sequences, adeno-associated virus-derived vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidosis type IVA or Morquio A syndrome.
priorityDate 2018-05-30-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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