http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3794125-A1

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publicationDate 2021-03-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3794125-A1
titleOfInvention Modified aav constructs and uses thereof
abstract In some aspects the disclosure relates to recombinant adeno-associated virus (rAAV) vectors and rAAVs (e.g., viral particles) engineered to express a transgene comprising an inhibitory nucleic acid (e.g., an artificial miRNA, amiRNA) having a pri-miRNA scaffold and a guide strand that targets a human target gene.
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01320
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68273
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9TTK8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01301
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01315
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15504
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID423437
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68275
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01314
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP84350
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68274
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP51608
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01298
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP84349
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68249
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7LZI4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30718
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68248
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23239
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01300
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID131890
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP84351
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01299
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226417154
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6DJ00
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID884179
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07310
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP49670
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32314
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29594
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403580
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100136352
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP28317
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID779340
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9NDE7
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419522148
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID54225
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542316
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6XGL2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396279
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02541
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17540
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP37999
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7059438
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226409524
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29577
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02540
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32100
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID324724
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP29120
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01340
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02542
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01339
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226409525
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395689
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF6PUF1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID379869
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4684
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01342
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID643460
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID443
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP09477
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33836
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01334
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226414067
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ3ZBP1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9GLR1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01331
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID373871
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281233
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01336
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID443006
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01335
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP10601
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA1A4R0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396725
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7456
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP09476
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5539
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6750
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP79780
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID25295
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48675
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C235
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID595015
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C236
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226536691
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID15891
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID43826
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP26460
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP31297
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA2D4U1
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06304
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5R7B5
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17661
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393895
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06305
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID69994

Total number of triples: 477.