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filingDate 2018-03-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b205f26559d2549b99bdf40d52f23395
publicationDate 2020-09-16-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3707265-A1
titleOfInvention Optimized aga genes and expression cassettes and their use
abstract This invention relates to polynucleotides comprising optimized aspartylglucosaminidase (AGA) open reading frames and vectors and cells comprising the same. The invention further relates to methods of using the same for delivery of the open reading frame to a cell or a subject and methods for treating aspartylglucosaminuria (AGU) in a subject.
priorityDate 2017-11-07-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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