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filingDate 2018-08-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_726a484ef071979eb2b5d49029b50407
publicationDate 2020-07-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3675836-A1
titleOfInvention Methods for treating muscular dystrophy
abstract The present invention relates, inter alia, to improved compositions and methods for treating muscular dystrophy. By way of example, the invention provides methods for treating patients with Duchenne muscular dystrophy having a DMD gene mutation that is capable of skipping exon 53 by administering an effective amount of golodirsen.
priorityDate 2017-08-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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