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filingDate 2018-05-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2020-03-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3622060-A1
titleOfInvention Sulfamidase (sgsh) variants, vectors, compositions and methods and uses for treating mucopolysaccharidosis type iiia (mps iiia)
abstract The invention relates to sulfamidase (SGSH) and SGSH variants. SGSH and SGSH variants can be delivered by way of a recombinant adeno-associated virus (rAAV) particle to a mammal's central nervous system (CNS) to transduce CNS cells that contact cerebrospinal fluid (CSF). Target mammals for SGSH and SGSH variant administration include mammals with a deficiency or defect in SGSH expression or function.
priorityDate 2017-05-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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