http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3481376-A1

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filingDate 2017-07-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_d8dcfa6b8a96df2dbb1a04ffbb6d9767
publicationDate 2019-05-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3481376-A1
titleOfInvention Compositions and methods of treating and/or preventing lysosomal storage diseases and other monogenetic metabolic diseases
abstract The present invention includes compositions for treating a lysosomal storage disease or disorder, and methods using same. In certain embodiments, the compositions of the invention comprise a histone deacetylase inhibitor (HDACi), a cyclodextrin, water, optionally a polyalkylene glycol, and optionally dimethyl sulfoxide (DMSO). In other embodiments, the compositions of the invention comprise a HDACi, a cyclodextrin, water, a polyalkylene glycol, and DMSO.
priorityDate 2016-07-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID565482
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID308909
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419499081
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27034
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID55590808
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Total number of triples: 414.