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publicationDate 2018-12-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3415167-A1
titleOfInvention Intrathecal delivery of recombinant adeno-associated virus 9
abstract The present invention relates to Adeno-associated virus type 9 methods and materials useful for intrathecal delivery of polynucleotides. Use of the methods and materials is indicated, for example, for treatment of lower motor neuron diseases such as SMA and ALS as well as Pompe disease and lysosomal storage disorders.
priorityDate 2012-08-01-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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