http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3394270-A1

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filingDate 2016-12-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_09fc4ac0c4e08cf51f4d4e410ec498d2
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publicationDate 2018-10-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3394270-A1
titleOfInvention Adeno-associated viral vectors useful in treatment of spinal muscular atropy
abstract Compositions and methods useful in treating spinal muscular atrophy are provided. The compositions comprise a recombinant adeno-associated viral vector containing an AAV capsid, e.g., AAVrh.10 capsid, and nucleic acid sequences encoding a functional SMN protein. The methods involve administering these compositions to humans in need thereof.
priorityDate 2015-12-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 516.