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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8a550628093367f7e91aa9ea9691f148
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publicationDate 2017-01-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3119888-A1
titleOfInvention Compositions for modulating ataxin 2 expression
abstract Disclosed herein are antisense compounds and methods for decreasing Ataxin 2 mRNA and protein expression. Such methods, compounds, and compositions are useful to treat, prevent, or ameliorate Ataxin 2 associated diseases, disorders, and conditions. Such Ataxin 2 associated diseases include spinocerebellar ataxia type 2 (SCA2), amyotropic sclerosis (ALS), and parkinsonism.
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http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11286485-B2
priorityDate 2014-03-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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