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filingDate 2014-12-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_361eac659f1eadffb2c213d83a402821
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publicationDate 2016-10-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3077520-A1
titleOfInvention Methods and pharmaceutical compositions for expressing a polynucleotide of interest in the retinal pigment epithelium of a subject
abstract The present invention relates to methods and pharmaceutical compositions for expressing a polynucleotide of interest in the retinal pigment epithelium of a subject. In particular, the present invention relates to a method for selectively expressing a polynucleotide of interest in the retinal pigment epithelium in an eye of a subject in need thereof comprising the step of transducing the retinal pigment epithelium with an amount of a rAAV2/5 vector containing the polynucleotide of interest.
priorityDate 2013-12-06-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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