http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-2442816-A1

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publicationDate 2012-04-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-2442816-A1
titleOfInvention Compositions and methods for modulation of smn2 splicing in a subject
abstract Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2 mRNA in a subject. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of diseases and disorders, including spinal muscular atrophy.
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