http://rdf.ncbi.nlm.nih.gov/pubchem/patent/CN-113785060-A

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filingDate 2020-04-01-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_50eb63467a452443687f57c51d0b487b
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publicationDate 2021-12-10-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber CN-113785060-A
titleOfInvention Oligonucleotides for modulating expression of ATXN2
abstract The present invention relates to antisense oligonucleotides capable of modulating the expression of ATXN2 in a target cell. The oligonucleotide hybridizes to ATXN2 mRNA. The invention further relates to conjugates and pharmaceutical compositions of said oligonucleotides, and methods of using said oligonucleotides for treating neurodegenerative diseases such as spinocerebellar ataxia type 2 (SCA2), Amyotrophic Lateral Sclerosis (ALS), alzheimer's disease frontotemporal dementia (FTD), parkinson's syndrome, and disorders with TDP-43 proteinopathies.
priorityDate 2019-04-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID317743
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP61880
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ48335
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID41883
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID22042
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID10080320
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8618300
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO14556
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2539643
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9KPX8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00761
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9541
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP46406
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100009074
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8EE30
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO28542
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID7037
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID30976
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ55801
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6029
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6YUU0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP83456
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO27090
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID9877416
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP83601
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A7Y4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04406
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID450716330

Total number of triples: 341.