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filingDate 2017-04-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b2761ec2c1bacb3e67b536bc1ee711a7
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b6d578abc12dcf399d18b2671206095d
publicationDate 2019-01-01-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber CN-109121395-A
titleOfInvention Adeno-associated virus vector delivery of β-sarcoglycan and microRNA-29 and treatment of muscular dystrophy
abstract Described herein are recombinant AAV vectors comprising polynucleotide sequences comprising β-sarcoglycan, and methods of using the recombinant vectors to reduce or prevent fibrosis in mammalian subjects with muscular dystrophy. Also described herein is a combination therapy comprising administering to a mammalian subject suffering from muscular dystrophy an AAV vector expressing β-sarcoglycan and miR-29c.
priorityDate 2016-04-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1R0H8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6P8J7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07916
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ91A21
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67970
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67969
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID67631909
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP30275
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6XGL2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP25809
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID783645
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5EA61
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ64727
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID524920
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ91493
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100171813
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID48445
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7M3Y3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP25477
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ98TA8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13405
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP08091

Total number of triples: 340.