abstract |
The present invention is provided to treat, delay and/or prevent the noval chemical compound of human genetic disease, human genetic disease type of myotonia dystrophy 1 as caused by the CUG Repeated expansions in the transcript as DM1/DMPK, SCA8 or JPH3 gene(DM1), the type of spinocebellar ataxia 8 and/or the type of Huntington's disease sample 2. |