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filingDate 2020-01-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_ab5461f3d95189a35857da6499629f1e
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b9e9b1b1b163a002e27e7b91f157be64
publicationDate 2020-07-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber CA-3126429-A1
titleOfInvention Aav gene therapy for treating nephrotic syndrome
abstract The present invention provides an adeno-associated virus (AAV) vector gene therapy for use in treating a monogenic form of nephrotic syndrome, wherein the AAV vector comprises a NS-associated transgene and minimal nephrin promoter NPHS1 or podocin promoter NPHS2.
priorityDate 2019-01-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP35564
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9995
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID43826
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2717
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID782183
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID571549
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID799071
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281040
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP35565
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42633
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID36800
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5R440
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID454031468
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01308
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID83478
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP79132

Total number of triples: 337.