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filingDate 2011-03-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_097ce1e7659f587b5e84f1664df4d715
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_841de7a871f9a616dd6fda3da1327deb
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publicationDate 2011-09-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber CA-2792696-A1
titleOfInvention Modified u7 snrnas for treatment of neuromuscular diseases
abstract The present invention relates to a method to improve the activity of engineered U7 snRNAs used in the context of RNA-based therapeutics; particularly in exon skipping, exon inclusion, and mRNA eradication strategies. The resulting modified U7 snRNAs are useful for treating neuromuscular diseases, in particular Duchenne neuromuscular dystrophy, myotonic dystrophy DM1 and spinal muscular atrophy.
priorityDate 2010-03-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23722
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP50321
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6P869
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01308
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP69047
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP69046
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ97BJ8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4WIW2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ673L6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP69045
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID374193
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XJ10
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19593
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68992
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9ZKT0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68991
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6YK33
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XFN2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68990
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13346
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100171813
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68989
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ971K2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XDW3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68988
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID852647
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO62654
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68987
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP47543
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2FNA2
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID447566935
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542367

Total number of triples: 350.