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publicationDate 2020-12-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber BR-112020012921-A2
titleOfInvention ALPHA-SINUCLEIN ANTISENSE OLIGONUCLEOTIDES AND USES THEREOF
abstract The present disclosure relates to antisense oligonucleotides, which target alpha-synuclein (SNCA) transcription in a cell leading to reduced SNCA protein expression. Reduction of SNCA protein expression is beneficial for the treatment of certain medical disorders, for example a neurological disorder such as a synucleinopathy.
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Total number of triples: 492.