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filingDate 2021-07-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_c3dbcb121949ff1c03c6af234a013175
publicationDate 2021-07-29-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2021204690-A1
titleOfInvention Compositions and methods for treating Leber's hereditary optic neuropathy
abstract Disclosed herein is a recombinant nucleic acid, comprising: a mitochondrial targeting nsequence; a mitochondrial protein coding sequence, wherein said mitochondrial protein coding nsequence encodes a polypeptide comprising a mitochondrial protein; and a 3'UTR nucleic acid nsequence. Also disclosed is a pharmaceutical composition comprising the recombinant nucleic acid nand a method of treating Leber's hereditary optic neuropathy (LHON) using the pharmaceutical ncomposition.
priorityDate 2018-06-29-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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Total number of triples: 1249.