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filingDate 2020-10-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_3f307bc82bba22c86571238e0ed4565b
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publicationDate 2020-11-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2020260387-A1
titleOfInvention Dystrophin gene exon deletion using engineered nucleases
abstract The invention relates to the field of molecular biology and recombinant nucleic nacid technology. In particular, the invention relates to a method of treating a patient with nDuchenne Muscular Dystrophy comprising the removal of at least one exon from the ndystrophin gene using engineered nucleases.
priorityDate 2014-03-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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