http://rdf.ncbi.nlm.nih.gov/pubchem/patent/AU-2020235121-A1

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filingDate 2020-03-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-11-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2020235121-A1
titleOfInvention Non-viral DNA vectors and uses thereof for expressing phenylalanine hydroxylase (PAH) therapeutics
abstract The application describes ceDNA vectors having linear and continuous structure for delivery and expression of a transgene. ceDNA vectors comprise an expression cassette flanked by two ITR sequences, where the expression cassette encodes a transgene encoding PAH protein. Some ceDNA vectors further comprise cis-regulatory elements, including regulatory switches. Further provided herein are methods and cell lines for reliable gene expression of PAH protein
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP55945
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ88UT1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID105468624
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07865
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ03181
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13164
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5265
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68563
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8674055
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13257
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID336542
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID23778904
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID406778
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID11461
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5YDB0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ65RN9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID7852
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID280813
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8658565
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13077
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07605
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9A7V7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP33802
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7TQD2
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419503830
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15419
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A5G2QRW3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ98D72
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13163
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6Y239
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3043
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO09232
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6437081
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5Y8S5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ65DU6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP33709
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135499568
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04407
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP10893
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67823
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07415
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9Q8N6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6XUW5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100499573
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC1FQ94
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID322701
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8Y4A7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ87QJ8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67824
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID937033
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07420
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ27957
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9ZIG2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100499574
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID368
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100038780
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID38871
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67819
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02075
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC1F0Q7
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID1406222
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67820
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID75293262
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02076
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP33708
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13649
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67821
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02084
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN27
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP67822
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02085
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID15452
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID171075
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ38WJ3
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO18473
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02073
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN22
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8626236
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7VQZ6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45025160
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68232
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN25
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403580
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02060
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN26

Total number of triples: 1127.