http://rdf.ncbi.nlm.nih.gov/pubchem/patent/AU-2020217708-A1

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filingDate 2020-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_aee9495d04cf95d8927b61969ff2bf24
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_703789f69dea7c379e42b5c996fa7146
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publicationDate 2021-08-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2020217708-A1
titleOfInvention Adeno-associated virus delivery of CLN3 polynucleotide
abstract The present disclosure relates to recombinant adeno-associated virus (rAAV) delivery of a ceroid lipofuscinosis neuronal 3 (CLN3) polynucleotide. The disclosure provides rAAV and methods of using the rAAV for CLN3 gene therapy of the neuronal ceroid lipofuscinosis or CLN3 -Batten Disease.
priorityDate 2019-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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