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filingDate 2019-07-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-03-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2019306236-A1
titleOfInvention Treatment of mucopolysaccharidosis I with fully-human glycosylated human alpha-L-iduronidase (IDUS)
abstract Compositions and methods are described for the delivery of a fully human-glycosylated (HuGly) α-L-iduronidase (IDUA) to the cerebrospinal fluid of the central nervous system (CNS) of a human subject diagnosed with mucopolysaccharidosis I (MPS I).
priorityDate 2018-07-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 592.