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filingDate 2019-06-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-01-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2019286386-A1
titleOfInvention Recombinant AAV vectors and methods of using the same
abstract The present disclosure relates to recombinant vectors expressing the human ND4 gene, methods of preparing recombinant vectors expressing the human ND4 gene, and uses thereof. Recombinant AAV2 vectors as disclosed herein are useful in treating Leber Hereditary Optic Neuroretinopathy (LHON), including ND4-related LHON.
priorityDate 2018-06-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100137310
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A5F4CSC0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP18985
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02073
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24440
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID101126932

Total number of triples: 328.