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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_2022088d13cddd9ca6da47eb5ebc528d
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publicationDate 2020-01-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2019283961-A1
titleOfInvention Exon skipping compositions for treating muscular dystrophy
abstract Abstract Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described.
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