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filingDate 2018-09-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_29724625b51ea730b56fcd46be64e61a
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publicationDate 2020-03-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2018337854-A1
titleOfInvention Thiomorpholino oligonucleotides for the treatment of muscular dystrophy
abstract Improved compositions and methods for treating muscular dystrophy by administering antisense thiomorpholino molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping to produce a functional Dystrophin protein.
priorityDate 2017-09-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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