http://rdf.ncbi.nlm.nih.gov/pubchem/patent/AU-2016231067-A1

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filingDate 2016-03-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_cb82b4398a8ac3729a15423ab1d55707
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publicationDate 2017-10-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2016231067-A1
titleOfInvention Oligonucleotides matching COL7A1 exon 73 for epidermolysis bullosa therapy
abstract Antisense oligonucleotides capable of preventing or reducing exon 73 inclusion into the human COL7A mRNA are characterized in various ways: (a) the oligonucleotide's sequence includes at most two CpG sequences; (b) the oligonucleotide has a length of no more than 24 nucleotides; (c) the oligonucleotide is capable of annealing to the (SRp40/SC35 binding / ESE) element in exon73. These oligonucleotides can usefully be oligoribonucleotides with modified internucleosidic linkages e.g. phosphorothioate linkages.
priorityDate 2015-03-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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