http://rdf.ncbi.nlm.nih.gov/pubchem/patent/AU-2015318782-A1

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filingDate 2015-09-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_28379dcd015e235c6581e23733270a90
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e0e330bf64fcec60f116b1789f4af284
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publicationDate 2017-04-06-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2015318782-A1
titleOfInvention Allele-specific therapy for Huntington Disease haplotypes
abstract The present invention relates to compositions and methods of use thereof for inhibiting mutant HTT mRNA transcription or CAG-expanded HTT protein expression in a cell, comprising contacting the cell with an effective amount of an oligomer targeting a differentiating polymorphism, wherein the differentiating polymorphism is selected from rs72239206, rs363107, rs362313, rs2530595, rs113407847. Specific oligomer sequences are also provided.
priorityDate 2014-09-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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