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filingDate 2014-06-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2020-05-21-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_89e2ed5c91d9c335807142fb7cf94e29
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_401934ce675e06ff9fb6655f49bfbe60
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publicationDate 2020-05-21-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2014281031-B2
titleOfInvention Delivery, use and therapeutic applications of the CRISPR-Cas systems and compositions for targeting disorders and diseases using viral components
abstract The invention provides for delivery, engineering and optimization of systems, methods, and compositions for manipulation of sequences and/or activities of target sequences. Provided are delivery systems and tissues or organ which are targeted as sites for delivery. Also provided are vectors and vector systems some of which encode one or more components of a CRISPR complex, as well as methods for the design and use of such vectors. Also provided are methods of directing CRISPR complex formation in eukaryotic cells to ensure enhanced specificity for target recognition and avoidance of toxicity and to edit or modify a target site in a genomic locus of interest to alter or improve the status of a disease or a condition.
priorityDate 2013-06-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 403.