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filingDate 2013-09-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2019-04-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_16763678ff87330c723d51880ff5c2e0
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publicationDate 2019-04-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber AU-2013319788-B2
titleOfInvention Restoration of the CFTR function by splicing modulation
abstract The present provides oligonucleotides capable of binding to and modulating the splicing of the pre-mRNA of the CFTR gene, compositions comprising said oligonucleotides, kits comprising said compositions, and uses thereof. In particular, the present invention provides compositions of oligonucleotides useful in methods for suppressing exon 10 skipping optionally in combination with additional CFTR therapeutics.
priorityDate 2012-09-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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