Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_15d42f684941d5b0617ca7764ebdff07 |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3233 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2320-32 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3513 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K47-64 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-712 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-54 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07K14-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61P21-00 |
filingDate |
2013-09-24-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationDate |
2015-04-29-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
AR-092658-A1 |
titleOfInvention |
OLIGONUCLEOTIDOS ANTISENTIDO MORFOLINO UNITED TO PEPTIDE FOR THE TREATMENT OF MYOTONIC DYSTROPHY |
abstract |
Peptide-bound morpholino antisense oligonucleotides (PPMO) are provided herein which are directed to the poly CUG repeat extension in the untranslated region 3 of the gene encoding the myotonic dystrophy kinase protein (DMPK) and methods for administration systemic system for the treatment of myotonic dystrophy type I (DM1). |
priorityDate |
2012-09-25-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |